Current Gene Therapy Trials

Clinical Trials For Genetic Eye Disorders

AAPOS has no financial interest in any clinical trials. AAPOS does not promote any particular study, and does not endorse any study. Clinical trials by definition offer treatments that have not been tested and may or may not benefit patients who enroll.

Partial list of treatment trials for children with genetic eye disorders.

Please refer to  for more information.

There are many more gene therapy trials for patients 18 years and older.

There is also a registry and natural history observational study for many retinal degenerations. For more information contact 1-800-683-555.  Free molecular genetic testing is also available for a large number of retinal genes through MyRetinaTracker; go to